marchiuse
- Oct 9, 2017
- 1 min
Gene therapy halts progression of cerebral adrenoleukodystrophy in clinical trial
Adrenoleukodystrophy — depicted in the 1992 movie “Lorenzo’s Oil” — is a genetic disease that most severely affects boys. Caused by a...
11 views
Defytime Emea
- Oct 5, 2017
- 1 min
Gene therapy shows promise for reversing blindness
Most causes of untreatable blindness occur due to loss of the millions of light sensitive photoreceptor cells that line the retina,...
4 views
Defytime Emea
- Sep 9, 2017
- 1 min
Researchers find shortened telomeres linked to dysfunction in Duchenne Muscular Dystrophy
Researchers from the Perelman School of Medicine at the University of Pennsylvania have made a discovery about muscular dystrophy...
14 views